#mecp2 — Public Fediverse posts
Live and recent posts from across the Fediverse tagged #mecp2, aggregated by home.social.
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FDA approval of trofinetide may spur further drug development for Rett
https://www.spectrumnews.org/news/fda-approval-of-trofinetide-may-spur-further-drug-development-for-rett/
#Rettsyndrome #mousemodels #treatments #autism #MECP2 #News -
Going on Trial: Orphan drugs; CBD; bumetanide
https://www.spectrumnews.org/news/going-on-trial-orphan-drugs-cbd-bumetanide/
#inhibitorysignaling #fragileXsyndrome #clinicaltrials #Rettsyndrome #genetherapy #mousemodels #funding #autism #22q11 #MECP2 #News #FMR1 -
Epigenome edits unmute MECP2 in Rett-like neurons
https://www.spectrumnews.org/news/epigenome-edits-unmute-mecp2-in-rett-like-neurons/
#Rettsyndrome #genetherapy #mousemodels #autism #MECP2 #News