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#genetherapy — Public Fediverse posts

Live and recent posts from across the Fediverse tagged #genetherapy, aggregated by home.social.

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  1. "Doctors took Mei for a full-body CT scan and then rushed her to the intensive care unit. Her brave face had begun to crack. 'Mom, I want to go home,' she told her mother, before vanishing into the ward."

    Brendan Borrell for Science and Retraction Watch: science.org/content/article/ex

    #Longreads #GeneEditing #GeneTherapy #Science #Medicine #China #Research

  2. "Doctors took Mei for a full-body CT scan and then rushed her to the intensive care unit. Her brave face had begun to crack. 'Mom, I want to go home,' she told her mother, before vanishing into the ward."

    Brendan Borrell for Science and Retraction Watch: science.org/content/article/ex

    #Longreads #GeneEditing #GeneTherapy #Science #Medicine #China #Research

  3. “Seven days after the girl’s medical team infused trillions of viruses carrying the recipe for the base editor into her spinal fluid, she died of a severe immune reaction linked to the therapy…”

    This is an important and tragic story. (It’s also an incredibly well reported one.)

    #genetherapy #trials #ethics

    science.org/content/article/ex

  4. “Seven days after the girl’s medical team infused trillions of viruses carrying the recipe for the base editor into her spinal fluid, she died of a severe immune reaction linked to the therapy…”

    This is an important and tragic story. (It’s also an incredibly well reported one.)

    #genetherapy #trials #ethics

    science.org/content/article/ex

  5. Sugar-Coated Nanoparticles Target Brain Tumors in Experimental Therapy

    📰 Original title: This sugar-coated therapy boosted survival against deadly brain cancer by 50% in mice

    🤖 IA: It's clickbait ⚠️
    👥 Users: It's clickbait ⚠️

    View full AI summary en.killbait.com/sugar-coated-n

    #science #genetherapy #braincancer #nanoparticles

  6. DATE: July 16, 2026 at 09:51PM
    SOURCE: SCIENCE DAILY MIND-BRAIN FEED

    TITLE: This sugar-coated therapy boosted survival against deadly brain cancer by 50% in mice

    URL: sciencedaily.com/releases/2026

    A new experimental treatment may have found a way to outsmart glioblastoma’s toughest defense: the blood-brain barrier. Researchers used sugar-coated nanoparticles to ferry genetic instructions that restore a key tumor-suppressing protein directly into brain cancer cells. In mouse studies, the therapy increased median survival by 50% while shrinking tumors without noticeable damage to other organs.

    URL: sciencedaily.com/releases/2026

    -------------------------------------------------

    Private, vetted email list for mental health professionals: clinicians-exchange.org

    Unofficial Psychology Today Xitter to toot feed at Psych Today Unofficial Bot @PTUnofficialBot

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    #psychology #counseling #socialwork #psychotherapy @psychotherapist @psychotherapists @psychology @socialpsych @socialwork @psychiatry #mentalhealth #psychiatry #healthcare #depression #psychotherapist #Glioblastoma #BloodBrainBarrier #NanoMedicine #SugarCoatedNanoparticles #GeneTherapy #TumorSuppressor #BrainCancerResearch #CancerTherapy #SurvivalRate #MedicalBreakthrough

  7. DATE: July 16, 2026 at 09:51PM
    SOURCE: SCIENCE DAILY MIND-BRAIN FEED

    TITLE: This sugar-coated therapy boosted survival against deadly brain cancer by 50% in mice

    URL: sciencedaily.com/releases/2026

    A new experimental treatment may have found a way to outsmart glioblastoma’s toughest defense: the blood-brain barrier. Researchers used sugar-coated nanoparticles to ferry genetic instructions that restore a key tumor-suppressing protein directly into brain cancer cells. In mouse studies, the therapy increased median survival by 50% while shrinking tumors without noticeable damage to other organs.

    URL: sciencedaily.com/releases/2026

    -------------------------------------------------

    Private, vetted email list for mental health professionals: clinicians-exchange.org

    Unofficial Psychology Today Xitter to toot feed at Psych Today Unofficial Bot @PTUnofficialBot

    -------------------------------------------------

    #psychology #counseling #socialwork #psychotherapy @psychotherapist @psychotherapists @psychology @socialpsych @socialwork @psychiatry #mentalhealth #psychiatry #healthcare #depression #psychotherapist #Glioblastoma #BloodBrainBarrier #NanoMedicine #SugarCoatedNanoparticles #GeneTherapy #TumorSuppressor #BrainCancerResearch #CancerTherapy #SurvivalRate #MedicalBreakthrough

  8. #GeneTherapy #HeartDisease

    "Gene therapies to fix failing hearts gain steam after years in the doldrums

    Treatments aim to bulk up failing hearts to restore their vigour — but can the field move on from past controversy?

    The first clinical trial aimed at growing new heart-muscle cells is now under way, and companies are developing at least four other regenerative gene therapies for heart conditions.

    'These are the first-in-human studies to take regeneration into the clinic,' says Andrew Baker, a gene-therapy researcher at the University of Edinburgh, UK, who is unaffiliated with the efforts. 'It’s a very exciting time.'

    But the excitement is tempered with caution. The mammalian heart is bad at repairing itself and 'is notoriously unwieldy when it comes to efforts to try to get it to regenerate', says Sean Wu, a cardiologist at Stanford University in California. Some scientists are unconvinced that the data underpinning the existing clinical trial show true regeneration in the form of cell division. And efforts to regenerate the heart are still haunted by a controversy that led to the retraction of at least a dozen papers and the closure of a high-profile laboratory.

    Developing a gene therapy in this field will be difficult, says Antonio Abbate, a cardiologist at the University of Virginia in Charlottesville. But 'we have to do research because, eventually, we’ll get it right'"

    archive.ph/UbQtS

  9. #GeneTherapy #HeartDisease

    "Gene therapies to fix failing hearts gain steam after years in the doldrums

    Treatments aim to bulk up failing hearts to restore their vigour — but can the field move on from past controversy?

    The first clinical trial aimed at growing new heart-muscle cells is now under way, and companies are developing at least four other regenerative gene therapies for heart conditions.

    'These are the first-in-human studies to take regeneration into the clinic,' says Andrew Baker, a gene-therapy researcher at the University of Edinburgh, UK, who is unaffiliated with the efforts. 'It’s a very exciting time.'

    But the excitement is tempered with caution. The mammalian heart is bad at repairing itself and 'is notoriously unwieldy when it comes to efforts to try to get it to regenerate', says Sean Wu, a cardiologist at Stanford University in California. Some scientists are unconvinced that the data underpinning the existing clinical trial show true regeneration in the form of cell division. And efforts to regenerate the heart are still haunted by a controversy that led to the retraction of at least a dozen papers and the closure of a high-profile laboratory.

    Developing a gene therapy in this field will be difficult, says Antonio Abbate, a cardiologist at the University of Virginia in Charlottesville. But 'we have to do research because, eventually, we’ll get it right'"

    archive.ph/UbQtS

  10. @feather1952 @Susan60 @Spoon
    This is why I find med research so incredibly hopeful (not unbiased here since my daughter is a human biology researcher). That we can identify genes/proteins which cause deadly and debilitating disorders and take precautions to mitigate their transmission if they cannot be switched off. That and the good fortune of living in a country (never ceded) where body autonomy is still acknowledged and not impinged on by batshit crazy religious zealots. I have reasons to be hopeful more can be done in the future.

    #Science #MedicalResearch #Proteonomics #GeneTherapy #Healthcare #HereditaryDisorders

  11. @feather1952 @Susan60 @Spoon
    This is why I find med research so incredibly hopeful (not unbiased here since my daughter is a human biology researcher). That we can identify genes/proteins which cause deadly and debilitating disorders and take precautions to mitigate their transmission if they cannot be switched off. That and the good fortune of living in a country (never ceded) where body autonomy is still acknowledged and not impinged on by batshit crazy religious zealots. I have reasons to be hopeful more can be done in the future.

    #Science #MedicalResearch #Proteonomics #GeneTherapy #Healthcare #HereditaryDisorders

  12. A Phase 1b clinical trial of Eli Lilly’s gene therapy VERVE-102 has shown up to 62% reduction in LDL cholesterol with a single dose, raising hopes for long-term treatment of hypercholesterolaemia and heart disease risk. english.mathrubhumi.com/lifest #GeneTherapy #BadCholesterol #Biotechnology #ClinicalTrial

  13. Eli Lilly is preparing a phase 2 trial for VERVE-102, a one-time gene editor acquired from Verve Therapeutics. The highest dose cut LDL cholesterol by 62% in patients, a reduction sustained for up to 18 months across 35 participants.

    The treatment permanently switches off PCSK9, a cholesterol-producing gene, using base editing that flips a single DNA letter without breaking the double helix.

    #news #health #medicine #cholesterol #GeneTherapy #GeneEditing

  14. Eli Lilly is preparing a phase 2 trial for VERVE-102, a one-time gene editor acquired from Verve Therapeutics. The highest dose cut LDL cholesterol by 62% in patients, a reduction sustained for up to 18 months across 35 participants.

    The treatment permanently switches off PCSK9, a cholesterol-producing gene, using base editing that flips a single DNA letter without breaking the double helix.

    #news #health #medicine #cholesterol #GeneTherapy #GeneEditing

  15. تحليل SWOT جديد لـ CRISPR Therapeutics يكشف عن ضغوط تنافسية قوية في قطاع العلاج الجيني. 🌟
    • **النقاط الرئيسية**: الشركة تواجه تحديات من المنافسين المحتملين، لكن فرص كبيرة في تطوير العلاجات الجينية المبتكرة.
    • **الخبرة المفيدة**: استثمر في البنية التحتية التكنولوجية وتابع تطورات القطاع.

    #CRISPR #GeneTherapy #Investing #Biotech #Tech

    🔗 news.google.com/rss/articles/C

  16. تحليل SWOT جديد لـ CRISPR Therapeutics يكشف عن ضغوط تنافسية قوية في قطاع العلاج الجيني. 🌟
    • **النقاط الرئيسية**: الشركة تواجه تحديات من المنافسين المحتملين، لكن فرص كبيرة في تطوير العلاجات الجينية المبتكرة.
    • **الخبرة المفيدة**: استثمر في البنية التحتية التكنولوجية وتابع تطورات القطاع.

    #CRISPR #GeneTherapy #Investing #Biotech #Tech

    🔗 news.google.com/rss/articles/C

  17. One infusion. One time. Possibly forever. A breakthrough gene-editing treatment just slashed LDL "bad" cholesterol by up to 62% — and the results are holding 18 months later. Published in the New England Journal of Medicine, the small study of 35 patients could reshape how we fight heart disease, which kills 800,000 Americans annually. No daily pills. No repeat treatments. Just one shot. Experts call it potentially "game-changing." Larger trials are next — but the early signs are extraordinary. The future of heart health may have just arrived. #HeartDisease #GeneTherapy #MedicalBreakthrough #Cholesterol #Health #Science #Medicine #NEJM #Innovation #Healthcare nytimes.com/2026/05/25/health/

  18. One infusion. One time. Possibly forever. A breakthrough gene-editing treatment just slashed LDL "bad" cholesterol by up to 62% — and the results are holding 18 months later. Published in the New England Journal of Medicine, the small study of 35 patients could reshape how we fight heart disease, which kills 800,000 Americans annually. No daily pills. No repeat treatments. Just one shot. Experts call it potentially "game-changing." Larger trials are next — but the early signs are extraordinary. The future of heart health may have just arrived. #HeartDisease #GeneTherapy #MedicalBreakthrough #Cholesterol #Health #Science #Medicine #NEJM #Innovation #Healthcare nytimes.com/2026/05/25/health/

  19. Adenine base editing, a highly targeted form of genetic medicine, has been successfully deployed in a preclinical mouse model to correct the specific DNA mutation (SCN1A) responsible for Dravet syndrome, a severe and often fatal form of childhood epilepsy.
    #MolecularGenetics #Neurobiology #GeneTherapy #PrecisionMedicine #sflorg
    sflorg.com/2026/05/gen05142601

  20. Adenine base editing, a highly targeted form of genetic medicine, has been successfully deployed in a preclinical mouse model to correct the specific DNA mutation (SCN1A) responsible for Dravet syndrome, a severe and often fatal form of childhood epilepsy.
    #MolecularGenetics #Neurobiology #GeneTherapy #PrecisionMedicine #sflorg
    sflorg.com/2026/05/gen05142601

  21. Researchers Identify Key Genes for Limb Regeneration in Animals

    📰 Original title: Scientists found the "holy grail" gene that could one day help humans regrow limbs

    🤖 IA: It's clickbait ⚠️
    👥 Users: It's clickbait ⚠️

    View full AI summary: killbait.com/en/researchers-id

    #genetics #genetherapy #regeneration #limbgrowth

  22. Researchers Identify Key Genes for Limb Regeneration in Animals

    📰 Original title: Scientists found the "holy grail" gene that could one day help humans regrow limbs

    🤖 IA: It's clickbait ⚠️
    👥 Users: It's clickbait ⚠️

    View full AI summary: killbait.com/en/researchers-id

    #genetics #genetherapy #regeneration #limbgrowth

  23. 🧠 Could the brain reveal vision loss more accurately than traditional eye tests?

    🔗 Using Steady-State Visual Evoked Potentials to Characterize Wide-Ranging Retinopathy Linked to CRB1: Implications for Clinical Trials. Computational and Structural Biotechnology Journal (CSBJ). DOI: doi.org/10.34133/csbj.0042

    📚 CSBJ - A Science Partner Journal: spj.science.org/journal/csbj

    #Neuroscience #Ophthalmology #RetinalDiseases #GeneTherapy #EEG #BrainResearch #DigitalHealth #PrecisionMedicine #Neuroimaging

  24. 🧠 Could the brain reveal vision loss more accurately than traditional eye tests?

    🔗 Using Steady-State Visual Evoked Potentials to Characterize Wide-Ranging Retinopathy Linked to CRB1: Implications for Clinical Trials. Computational and Structural Biotechnology Journal (CSBJ). DOI: doi.org/10.34133/csbj.0042

    📚 CSBJ - A Science Partner Journal: spj.science.org/journal/csbj

    #Neuroscience #Ophthalmology #RetinalDiseases #GeneTherapy #EEG #BrainResearch #DigitalHealth #PrecisionMedicine #Neuroimaging

  25. 👂🧬 The #FDA approved #Otarmeni, the first gene therapy designed to restore #hearing in individuals with a rare form of genetic #deafness caused by OTOF gene mutations.

    The one-time treatment delivers a functional copy of the gene into the inner ear, enabling cells to transmit #sound signals to the #brain.

    👉 livescience.com/health/genetic

    #genetics #health #science #biology #medicine #biotechnology #research #genetherapy #innovation

  26. 👂🧬 The #FDA approved #Otarmeni, the first gene therapy designed to restore #hearing in individuals with a rare form of genetic #deafness caused by OTOF gene mutations.

    The one-time treatment delivers a functional copy of the gene into the inner ear, enabling cells to transmit #sound signals to the #brain.

    👉 livescience.com/health/genetic

    #genetics #health #science #biology #medicine #biotechnology #research #genetherapy #innovation

  27. Gene therapy helps restore vision in six-year-old girl with rare genetic condition

    📰 Original title: Six-year-old girl has sight restored by first-of-a-kind gene therapy

    🤖 IA: It's not clickbait ✅
    👥 Usuarios: It's not clickbait ✅

    View full AI summary: killbait.com/en/gene-therapy-h

    #genetics #genetherapy