#duchennemusculardystrophy — Public Fediverse posts
Live and recent posts from across the Fediverse tagged #duchennemusculardystrophy, aggregated by home.social.
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https://www.europesays.com/ch/97327/ Novartis delpacibart braxlosiran (del-brax) Phase I/II study in facioscapulohumeral muscular dystrophy (FSHD) meets primary biomarker endpoint #ClinicalStudies #DuchenneMuscularDystrophy #FSHD #MuscleDamage #MuscularDystrophy #NeuromuscularDisease #Novartis #patients #PhaseIII #PhaseIIITrial #SpinalMuscularAtrophy
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Designer featured on Gardening Australia stripped of NDIS support funding
A Central Victorian man says the National Disability Insurance Agency (NDIA) has robbed him of dignity and is…
#Australia #AU #Austrlia #DuchenneMuscularDystrophy #garden #gardeningaustralia #joshuaruff #nationaldisabilityinsurancescheme #ndia #wheelchair
https://www.europesays.com/australia/40371/ -
Designer featured on Gardening Australia stripped of NDIS support funding
A Central Victorian man says the National Disability Insurance Agency (NDIA) has robbed him of dignity and is…
#NewsBeep #News #Sports #AU #Australia #duchennemusculardystrophy #Garden #GardeningAustralia #joshuaruff #nationaldisabilityinsurancescheme #ndia #sports #Wheelchair
https://www.newsbeep.com/au/766710/ -
Designer featured on Gardening Australia stripped of NDIS support funding
A Central Victorian man says the National Disability Insurance Agency (NDIA) has robbed him of dignity and is…
#NewsBeep #News #Sports #AU #Australia #duchennemusculardystrophy #Garden #GardeningAustralia #joshuaruff #nationaldisabilityinsurancescheme #ndia #sports #Wheelchair
https://www.newsbeep.com/au/766710/ -
Designer featured on Gardening Australia stripped of NDIS support funding https://www.allforgardening.com/1846147/designer-featured-on-gardening-australia-stripped-of-ndis-support-funding/ #DuchenneMuscularDystrophy #garden #gardening #GardeningAustralia #JoshuaRuff #NationalDisabilityInsuranceScheme #NDIA #wheelchair
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Designer featured on Gardening Australia stripped of NDIS support funding https://www.allforgardening.com/1846147/designer-featured-on-gardening-australia-stripped-of-ndis-support-funding/ #DuchenneMuscularDystrophy #garden #gardening #GardeningAustralia #JoshuaRuff #NationalDisabilityInsuranceScheme #NDIA #wheelchair
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https://www.europesays.com/ch/86498/ Roche to launch another Elevidys study, eying EU approval #Cell&GeneTherapy #Duchenne #DuchenneMuscularDystrophy(DMD) #Elevidys #EuropeanMedicinesAgency #FiercePharmaHomepage #GeneTherapy #Pharma #Roche #SareptaTherapeutics
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https://www.europesays.com/ch/83342/ Novartis delpacibart braxlosiran (del-brax) Phase I/II study in facioscapulohumeral muscular dystrophy (FSHD) meets primary biomarker endpoint #ClinicalStudies #DuchenneMuscularDystrophy #FSHD #MuscleDamage #MuscularDystrophy #NeuromuscularDisease #Novartis #patients #PhaseIII #PhaseIIITrial #SpinalMuscularAtrophy
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https://www.europesays.com/ch/81803/ Novartis Reports Positive Data for Neuromuscular Disorder Drug #CreatineKinase #DuchenneMuscularDystrophy #FSHD #GeneTherapy #MuscleDamage #MuscularDystrophy #Novartis #PhaseIIITrial #ZacksInvestmentResearch
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https://www.europesays.com/ch/81262/ Novartis delpacibart braxlosiran (del-brax) Phase I/II study in facioscapulohumeral muscular dystrophy (FSHD) meets primary biomarker endpoint #ClinicalStudies #DuchenneMuscularDystrophy #FSHD #MuscleDamage #MuscularDystrophy #NeuromuscularDisease #Novartis #patients #PhaseIII #PhaseIIITrial #SpinalMuscularAtrophy
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They thought their son lived an isolated life. But when he died, friends showed up in droves.
https://fed.brid.gy/r/https://www.upworthy.com/mats-steen-ibelin-world-of-warcraft-ex1
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They thought their son lived an isolated life. But when he died, friends showed up in droves.
https://web.brid.gy/r/https://www.upworthy.com/mats-steen-ibelin-world-of-warcraft-ex1
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They thought their son lived an isolated life. But when he died, friends showed up in droves.
https://web.brid.gy/r/https://www.upworthy.com/mats-steen-ibelin-world-of-warcraft-ex1
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They thought their son lived an isolated life. But when he died, friends showed up in droves.
https://web.brid.gy/r/https://www.upworthy.com/mats-steen-ibelin-world-of-warcraft-ex1
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Top FDA official overrules staff to approve gene therapy that failed trial - Enlarge / Dr. Peter Marks, Director of the Center for Biologics Evaluat... - https://arstechnica.com/?p=2032919 #duchennemusculardystrophy #clinicaltrials #clinicaldata #fdaapproval #genetherapy #petermarks #elevidys #science #sarepta #fda
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Top FDA official overrules staff to approve gene therapy that failed trial - Enlarge / Dr. Peter Marks, Director of the Center for Biologics Evaluat... - https://arstechnica.com/?p=2032919 #duchennemusculardystrophy #clinicaltrials #clinicaldata #fdaapproval #genetherapy #petermarks #elevidys #science #sarepta #fda
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Top FDA official overrules staff to approve gene therapy that failed trial - Enlarge / Dr. Peter Marks, Director of the Center for Biologics Evaluat... - https://arstechnica.com/?p=2032919 #duchennemusculardystrophy #clinicaltrials #clinicaldata #fdaapproval #genetherapy #petermarks #elevidys #science #sarepta #fda
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Top FDA official overrules staff to approve gene therapy that failed trial - Enlarge / Dr. Peter Marks, Director of the Center for Biologics Evaluat... - https://arstechnica.com/?p=2032919 #duchennemusculardystrophy #clinicaltrials #clinicaldata #fdaapproval #genetherapy #petermarks #elevidys #science #sarepta #fda
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Top FDA official overrules staff to approve gene therapy that failed trial - Enlarge / Dr. Peter Marks, Director of the Center for Biologics Evaluat... - https://arstechnica.com/?p=2032919 #duchennemusculardystrophy #clinicaltrials #clinicaldata #fdaapproval #genetherapy #petermarks #elevidys #science #sarepta #fda
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Thrilled to share our story on the first rationally designed #covalent #HDAC inhibitor! YSR734 uses an SNAr-reactive electrophile to engage a noncatalytic nitrosylation site cysteine in #HDAC2, showing in vitro activity in AML & #DuchenneMuscularDystrophy!
https://pubs.acs.org/doi/10.1021/acs.jmedchem.3c01236