#duchennemusculardystrophy — Public Fediverse posts
Live and recent posts from across the Fediverse tagged #duchennemusculardystrophy, aggregated by home.social.
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https://www.europesays.com/ch/51103/ Roche plots route to EMA approval for DMD gene therapy #BioWorld #ChugaiPharmaceuticalCoLtd #DuchenneMuscularDystrophy #Elevidys #EMA #Europe #GeneTherapy #JAPAN #Musculoskeletal #Regulatory #Roche #RocheAG #SareptaTherapeuticsInc
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They thought their son lived an isolated life. But when he died, friends showed up in droves.
https://web.brid.gy/r/https://www.upworthy.com/mats-steen-ibelin-world-of-warcraft-ex1
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Satellos to Present DMD Drug SAT-3247 Phase 1b Data at WMS 2025
09/29/2025…
#NewsBeep #News #US #USA #UnitedStates #UnitedStatesOfAmerica #BreakingNews #biotechnology #clinicaldata #DMD #duchennemusculardystrophy #FrankGleeson #Headlines #MSCLF #musclerepair #Phase1bclinicaltrial #SAT-3247 #Satellos #Topstories #TopStories #WildonFarwell #WMS2025 #WorldMuscleSocietyCongress
https://www.newsbeep.com/us/189681/ -
Satellos to Present DMD Drug SAT-3247 Phase 1b Data at WMS 2025
09/29/2025…
#NewsBeep #News #US #USA #UnitedStates #UnitedStatesOfAmerica #BreakingNews #biotechnology #clinicaldata #DMD #duchennemusculardystrophy #FrankGleeson #Headlines #MSCLF #musclerepair #Phase1bclinicaltrial #SAT-3247 #Satellos #Topstories #TopStories #WildonFarwell #WMS2025 #WorldMuscleSocietyCongress
https://www.newsbeep.com/us/189681/ -
New DMD Therapy Inhibits Glutamate Dehydrogenase 1
Credit: Sinhyu / iStock / Getty Images Plus Researchers at the VIB-KU Leuven Center for Brain and Disease…
#NewsBeep #News #US #USA #UnitedStates #UnitedStatesOfAmerica #Genetics #duchennemusculardystrophy #enzymes #muscles #news&features #Patientcare #pharmacology #Science #topics #translationalresearch
https://www.newsbeep.com/us/21194/ -
Top FDA official overrules staff to approve gene therapy that failed trial - Enlarge / Dr. Peter Marks, Director of the Center for Biologics Evaluat... - https://arstechnica.com/?p=2032919 #duchennemusculardystrophy #clinicaltrials #clinicaldata #fdaapproval #genetherapy #petermarks #elevidys #science #sarepta #fda
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Thrilled to share our story on the first rationally designed #covalent #HDAC inhibitor! YSR734 uses an SNAr-reactive electrophile to engage a noncatalytic nitrosylation site cysteine in #HDAC2, showing in vitro activity in AML & #DuchenneMuscularDystrophy!
https://pubs.acs.org/doi/10.1021/acs.jmedchem.3c01236