#duchennemusculardystrophy — Public Fediverse posts
Live and recent posts from across the Fediverse tagged #duchennemusculardystrophy, aggregated by home.social.
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Designer featured on Gardening Australia stripped of NDIS support funding https://www.allforgardening.com/1846147/designer-featured-on-gardening-australia-stripped-of-ndis-support-funding/ #DuchenneMuscularDystrophy #garden #gardening #GardeningAustralia #JoshuaRuff #NationalDisabilityInsuranceScheme #NDIA #wheelchair
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Designer featured on Gardening Australia stripped of NDIS support funding https://www.allforgardening.com/1846147/designer-featured-on-gardening-australia-stripped-of-ndis-support-funding/ #DuchenneMuscularDystrophy #garden #gardening #GardeningAustralia #JoshuaRuff #NationalDisabilityInsuranceScheme #NDIA #wheelchair
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The structure of spectrin-like repeat 24 of human dystrophin is in excellent agreement with the AlphaFold model, supporting AlphaFold modeling of all 24 dystrophin spectrin-like repeats #Dystrophin #SpectrinLikeRepeat #DuchenneMuscularDystrophy https://doi.org/10.1107/S2053230X26003262
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They thought their son lived an isolated life. But when he died, friends showed up in droves.
https://web.brid.gy/r/https://www.upworthy.com/mats-steen-ibelin-world-of-warcraft-ex1
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They thought their son lived an isolated life. But when he died, friends showed up in droves.
https://web.brid.gy/r/https://www.upworthy.com/mats-steen-ibelin-world-of-warcraft-ex1
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New DMD Therapy Inhibits Glutamate Dehydrogenase 1
Credit: Sinhyu / iStock / Getty Images Plus Researchers at the VIB-KU Leuven Center for Brain and Disease…
#NewsBeep #News #US #USA #UnitedStates #UnitedStatesOfAmerica #Genetics #duchennemusculardystrophy #enzymes #muscles #news&features #Patientcare #pharmacology #Science #topics #translationalresearch
https://www.newsbeep.com/us/21194/ -
Top FDA official overrules staff to approve gene therapy that failed trial - Enlarge / Dr. Peter Marks, Director of the Center for Biologics Evaluat... - https://arstechnica.com/?p=2032919 #duchennemusculardystrophy #clinicaltrials #clinicaldata #fdaapproval #genetherapy #petermarks #elevidys #science #sarepta #fda
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Top FDA official overrules staff to approve gene therapy that failed trial - Enlarge / Dr. Peter Marks, Director of the Center for Biologics Evaluat... - https://arstechnica.com/?p=2032919 #duchennemusculardystrophy #clinicaltrials #clinicaldata #fdaapproval #genetherapy #petermarks #elevidys #science #sarepta #fda
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Thrilled to share our story on the first rationally designed #covalent #HDAC inhibitor! YSR734 uses an SNAr-reactive electrophile to engage a noncatalytic nitrosylation site cysteine in #HDAC2, showing in vitro activity in AML & #DuchenneMuscularDystrophy!
https://pubs.acs.org/doi/10.1021/acs.jmedchem.3c01236 -
Data Support Placebo Group Alternatives in Rare Disease Trials
Findings from a review of medical #data and #records indicate matched #genetic control groups may not be needed in clinical trials testing treatments for Duchenne muscular dystrophy.
https://sciencebusiness.technewslit.com/?p=44426
#News #Science #Business #ClinicalTrials #DuchenneMuscularDystrophy #Neuroscience #Neurology #ControlGroup #Placebo #Statistics #RareDisease #InheritedDisease #RealWorldData
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Data Support Placebo Group Alternatives in Rare Disease Trials
Findings from a review of medical #data and #records indicate matched #genetic control groups may not be needed in clinical trials testing treatments for Duchenne muscular dystrophy.
https://sciencebusiness.technewslit.com/?p=44426
#News #Science #Business #ClinicalTrials #DuchenneMuscularDystrophy #Neuroscience #Neurology #ControlGroup #Placebo #Statistics #RareDisease #InheritedDisease #RealWorldData
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Huge thanks @ElectricWill for your wonderful donation 🙌🏻 to our fundraising campaign for #DuchenneMuscularDystrophy
I’m really looking forward to connecting with you more on here!
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Huge thanks @ElectricWill for your wonderful donation 🙌🏻 to our fundraising campaign for #DuchenneMuscularDystrophy
I’m really looking forward to connecting with you more on here!
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Our family has a young friend with #DuchenneMuscularDystrophy. We fundraise to help find a cure, - currently believed to be imminent enough to save many thousands of lives.
Each of my children has taken on a challenge to help. Last year, my 11 year-old walked the 102 mile #CotswoldWay. Thanks to people’s incredible generosity, he raised £10k for #DuchenneUK!
I am so proud of him ❤️
I would be so grateful if you could boost this to help us raise awareness. Thank you!
*More info in ALT text*
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Our family has a young friend with #DuchenneMuscularDystrophy. We fundraise to help find a cure, - currently believed to be imminent enough to save many thousands of lives.
Each of my children has taken on a challenge to help. Last year, my 11 year-old walked the 102 mile #CotswoldWay. Thanks to people’s incredible generosity, he raised £10k for #DuchenneUK!
I am so proud of him ❤️
I would be so grateful if you could boost this to help us raise awareness. Thank you!
*More info in ALT text*