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#inheriteddisease — Public Fediverse posts

Live and recent posts from across the Fediverse tagged #inheriteddisease, aggregated by home.social.

  1. Alan Kotok @[email protected] ·

    A new company spun-off from a university lab consortium is advancing gene therapies delivered through the lungs to treat rare inherited respiratory diseases.

    sciencebusiness.technewslit.co

    #News #Press #Science #Business #Biotechnology #StartUp #GeneTherapy #Respiratory #InheritedDisease #CysticFibrosis #AATD #Lentivirus #Aerosol #Nebulizer #Lungs #Finance #VentureCapital #Investment #SeedFunds #UK #University #Consortium #Labs

    #news #press #science #business #biotechnology #startup
  2. Alan Kotok @[email protected] ·

    Data Support Placebo Group Alternatives in Rare Disease Trials

    Findings from a review of medical #data and #records indicate matched #genetic control groups may not be needed in clinical trials testing treatments for Duchenne muscular dystrophy.

    sciencebusiness.technewslit.co

    #News #Science #Business #ClinicalTrials #DuchenneMuscularDystrophy #Neuroscience #Neurology #ControlGroup #Placebo #Statistics #RareDisease #InheritedDisease #RealWorldData

    #data #records #genetic #news #science #business