#rarediseases — Public Fediverse posts

Soligenix advances rare disease innovation using platform science to expand its therapeutic pipeline and address unmet medical needs affecting millions. #RareDiseases #Biotech

Soligenix reports strong Phase 3 HyBryte data for cutaneous T-cell lymphoma, with response rates exceeding expectations. Interim analysis could accelerate commercialization path. #Biotech #RareDiseases

Soligenix publishes peer-reviewed HyBryte clinical data demonstrating safety and efficacy for cutaneous T-cell lymphoma treatment. Phase 3 trial interim results expected Q2 2026. #Biotech #RareDiseases

Soligenix publishes HyBryte clinical data in peer-reviewed journal, highlighting safety and efficacy for cutaneous T-cell lymphoma treatment. Phase 3 interim analysis expected Q2 2026. #Biotech #RareDiseases

Soligenix's SGX945 receives Promising Innovative Medicine designation from UK MHRA for Behçet's disease, advancing rare disease treatment development. #Biotech #RareDiseases

Soligenix approaches pivotal 2026 with Phase 3 HyBryte trial for CTCL and SGX945 advancement for Behçet's disease. Multiple clinical catalysts expected. #Biotech #RareDiseases

Soligenix enters a pivotal 2026 with key clinical milestones ahead, including Phase 3 FLASH2 trial data for HyBryte in CTCL treatment and progress on SGX945 for Behçet's disease. #Biotech #RareDiseases

Soligenix receives European Commission orphan drug designation for SGX945 in Behçet's disease treatment, validating its rare disease pipeline strategy. #Biotech #RareDiseases

Soligenix receives European Commission orphan drug designation for SGX945 in Behçet's disease treatment, validating its rare disease pipeline strategy. #Biotech #RareDiseases

Soligenix receives European Commission orphan drug designation for SGX945 in Behçet's disease treatment, validating its rare disease pipeline strategy. #Biotech #RareDiseases

Soligenix receives European Commission orphan drug designation for SGX945 in Behçet's disease treatment, validating its rare disease pipeline strategy. #Biotech #RareDiseases

Soligenix receives European Commission orphan drug designation for SGX945 in Behçet's disease treatment, validating its rare disease pipeline strategy. #Biotech #RareDiseases

https://www.europesays.com/news/28725/ Regenxbio says Duchenne gene therapy succeeded in clinical trial #biotechnology #DrugDevelopment #Headlines #News #Pharmaceuticals #RareDiseases #STAT+ #TopStories

Soligenix reports positive Phase 2 trial results for SGX945 in treating Behçet's disease, offering new hope for patients with rare inflammatory condition #MedicalResearch #RareDiseases

Soligenix reports positive Phase 2 trial results for SGX945 in treating Behçet's disease, offering new hope for patients with rare inflammatory condition #MedicalResearch #RareDiseases

Soligenix reports positive Phase 2 trial results for SGX945 in treating Behçet's disease, offering new hope for patients with rare inflammatory condition #MedicalResearch #RareDiseases

Soligenix reports positive Phase 2 trial results for SGX945 in treating Behçet's disease, offering new hope for patients with rare inflammatory condition #MedicalResearch #RareDiseases

Soligenix reports positive Phase 2 trial results for SGX945 in treating Behçet's disease, offering new hope for patients with rare inflammatory condition #MedicalResearch #RareDiseases

Soligenix reports positive Phase 2 trial results for SGX945 in treating Behçet's disease, offering new hope for patients with rare inflammatory condition #MedicalResearch #RareDiseases

https://www.europesays.com/news/26885/ Passengers being evacuated from hantavirus ship at Tenerife – POLITICO #Belgium #France #Germany #GlobalHealth #Headlines #InfectiousDiseases #Ireland #News #Ports #PublicHealth #RareDiseases #TedrosAdhanomGhebreyesus #TheNetherlands #TopStories #UnitedKingdom #UnitedStates

Passengers begin leaving hantavirus ship at Tenerife – POLITICO

Spanish Health Minister Mónica García said the disembarkation was “proceeding normally” and that all passengers on board the…
#Spain #ES #Europe #Europa #EU #Belgium #France #Germany #globalhealth #infectiousdiseases #ireland #Ports #PublicHealth #Rarediseases #TedrosAdhanomGhebreyesus #TheNetherlands #UnitedKingdom #unitedstates
https://www.europesays.com/spain/20578/

Gotta try to get back #sleep. I ache all over right now Nurse gave me atarax and norco tonight to help. Good night to all. 1231 am in the PNW. #Insomnis&Pain sucks. #ChronicIllness #ChronicPain #RareDiseases I am a #zebra

siRNA Duplexes Market in Germany | Report – IndexBox

#Germany #DE #Europe #EU #Europa #BioinformaticsforsiRNAdesign&off-targetprediction #biopharmamarketreport #Chemicalmodificationchemistries #forecast #Genefunctionstudies #High-throughputgeneticscreening #High-throughputpurification&QC(HPLC #marketanalysis #MS) #rarediseases) #siRNAduplexes #Solid-phaseoligonucleotidesynthesis #Targetidentification/validation #Therapeuticcandidatedevelopment(oncology
https://www.europesays.com/germany/11517/

https://www.europesays.com/news/21622/ Intellia Therapeutics moves HAE treatment closer to approval #biotechnology #CRISPR #DrugDevelopment #FDA #GeneEditing #Headlines #News #RareDiseases #STAT+ #TopStories

https://www.europesays.com/ch/54951/ Novartis receives positive CHMP opinion for Itvisma® for #CellAndGeneTherapy #MediaRelease #Neuroscience #Novartis #NovartisPharmaAG #RareDiseases #ReimagineMedicine #SwissStockExchange:NOVNSW

This is the first step to do the amazing at CSL Plasma. Your help is essential to create life-saving medicines for patients in need. Use my link and we both get rewarded.
https://rewards.cslplasma.com/referral/referral-unique-code/eyJkb25vcklEIjoiMDBFQzNTOSIsImNvZGUiOiI5OU1GN0JNS1ZEIiwicmVnaW9uU2hvcnROYW1lIjoidXMifQ

#CSL #Donate #DonatePlasma #PlasmaDonation
#PlasmaDonor #SaveLives #BloodPlasma #GivePlasma #BeAHero
#CommunitySupport #MakeADifference #HelpOthers
#PayItForward #PlasmaTherapy
#MedicalResearch
#ChronicIllnessSupport #Healthcare
#RareDiseases #SideHustle #ExtraCash #PaidToSaveLives

This is the first step to do the amazing at CSL Plasma. Your help is essential to create life-saving medicines for patients in need. Use my link and we both get rewarded.
https://rewards.cslplasma.com/referral/referral-unique-code/eyJkb25vcklEIjoiMDBFQzNTOSIsImNvZGUiOiI5OU1GN0JNS1ZEIiwicmVnaW9uU2hvcnROYW1lIjoidXMifQ

#CSL #Donate #DonatePlasma #PlasmaDonation
#PlasmaDonor #SaveLives #BloodPlasma #GivePlasma #BeAHero
#CommunitySupport #MakeADifference #HelpOthers
#PayItForward #PlasmaTherapy
#MedicalResearch
#ChronicIllnessSupport #Healthcare
#RareDiseases #SideHustle #ExtraCash #PaidToSaveLives

This is the first step to do the amazing at CSL Plasma. Your help is essential to create life-saving medicines for patients in need. Use my link and we both get rewarded.
https://rewards.cslplasma.com/referral/referral-unique-code/eyJkb25vcklEIjoiMDBFQzNTOSIsImNvZGUiOiI5OU1GN0JNS1ZEIiwicmVnaW9uU2hvcnROYW1lIjoidXMifQ

#CSL #Donate #DonatePlasma #PlasmaDonation
#PlasmaDonor #SaveLives #BloodPlasma #GivePlasma #BeAHero
#CommunitySupport #MakeADifference #HelpOthers
#PayItForward #PlasmaTherapy
#MedicalResearch
#ChronicIllnessSupport #Healthcare
#RareDiseases #SideHustle #ExtraCash #PaidToSaveLives

This is the first step to do the amazing at CSL Plasma. Your help is essential to create life-saving medicines for patients in need. Use my link and we both get rewarded.
https://rewards.cslplasma.com/referral/referral-unique-code/eyJkb25vcklEIjoiMDBFQzNTOSIsImNvZGUiOiI5OU1GN0JNS1ZEIiwicmVnaW9uU2hvcnROYW1lIjoidXMifQ

#CSL #Donate #DonatePlasma #PlasmaDonation
#PlasmaDonor #SaveLives #BloodPlasma #GivePlasma #BeAHero
#CommunitySupport #MakeADifference #HelpOthers
#PayItForward #PlasmaTherapy
#MedicalResearch
#ChronicIllnessSupport #Healthcare
#RareDiseases #SideHustle #ExtraCash #PaidToSaveLives

This is the first step to do the amazing at CSL Plasma. Your help is essential to create life-saving medicines for patients in need. Use my link and we both get rewarded.
https://rewards.cslplasma.com/referral/referral-unique-code/eyJkb25vcklEIjoiMDBFQzNTOSIsImNvZGUiOiI5OU1GN0JNS1ZEIiwicmVnaW9uU2hvcnROYW1lIjoidXMifQ

#CSL #Donate #DonatePlasma #PlasmaDonation
#PlasmaDonor #SaveLives #BloodPlasma #GivePlasma #BeAHero
#CommunitySupport #MakeADifference #HelpOthers
#PayItForward #PlasmaTherapy
#MedicalResearch
#ChronicIllnessSupport #Healthcare
#RareDiseases #SideHustle #ExtraCash #PaidToSaveLives

Crowds could trigger Celine Dion during comeback, according to patient with her disease

NEWYou can now listen to Fox News articles! A former marathon runner who was diagnosed with the same…
#NewsBeep #News #Music #ALS #CelineDion #Entertainment #Health #Lifestyle #Rarediseases #stressandanxiety #UK #UnitedKingdom
https://www.newsbeep.com/uk/518258/

https://www.europesays.com/ch/?p=44311 Novartis IgAN data in New England Journal of Medicine show #ClinicalTrials #MediaRelease #Novartis #NovartisPharmaAG #RareDiseases #ReimagineMedicine #SwissStockExchange:NOVNSW

Boy’s heart stops for 16 minutes after tube comes loose in Hong Kong hospital

A probe has been launched into a serious medical incident in which a six‑year‑old boy’s heart stopped for…
#NewsBeep #News #Healthcare #asystole #AU #Australia #breathingtube #endotrachealtube #Health #heartbeats #HongKongChildren’sHospital #medicalblunder #paediatricintensivecareunit #RareDiseases #SinNgai‑chuen
https://www.newsbeep.com/au/584267/

Boy’s heart stops for 16 minutes after tube comes loose in Hong Kong hospital

A probe has been launched into a serious medical incident in which a six‑year‑old boy’s heart stopped for…
#NewsBeep #News #Healthcare #asystole #AU #Australia #breathingtube #endotrachealtube #Health #heartbeats #HongKongChildren’sHospital #medicalblunder #paediatricintensivecareunit #RareDiseases #SinNgai‑chuen
https://www.newsbeep.com/au/584267/

Wir starten in die letzte Inhalationswoche.

Dank den Frühlingsferien müssen wir wenigstens nicht schon 6 oder 7 Uhr anfangen. Also schaffen wir das doch locker 💪😆

#inhalation #antibiotikum #ataxiateleangiectasia #lungenkrankheit #rarediseases

Wir starten in die letzte Inhalationswoche.

Dank den Frühlingsferien müssen wir wenigstens nicht schon 6 oder 7 Uhr anfangen. Also schaffen wir das doch locker 💪😆

#inhalation #antibiotikum #ataxiateleangiectasia #lungenkrankheit #rarediseases

Wir starten in die letzte Inhalationswoche.

Dank den Frühlingsferien müssen wir wenigstens nicht schon 6 oder 7 Uhr anfangen. Also schaffen wir das doch locker 💪😆

#inhalation #antibiotikum #ataxiateleangiectasia #lungenkrankheit #rarediseases

The four types of dementia most people don’t know exist
#Dementia #HealthAwareness #BrainHealth #Alzheimers #Neurology #MedicalEducation #PublicHealth #RareDiseases #MentalHealth #Healthcare #Awareness #Science #Caregiving #Aging
https://the-14.com/the-four-types-of-dementia-most-people-dont-know-exist/

The four types of dementia most people don’t know exist
#Dementia #HealthAwareness #BrainHealth #Alzheimers #Neurology #MedicalEducation #PublicHealth #RareDiseases #MentalHealth #Healthcare #Awareness #Science #Caregiving #Aging
https://the-14.com/the-four-types-of-dementia-most-people-dont-know-exist/

The four types of dementia most people don’t know exist
#Dementia #HealthAwareness #BrainHealth #Alzheimers #Neurology #MedicalEducation #PublicHealth #RareDiseases #MentalHealth #Healthcare #Awareness #Science #Caregiving #Aging
https://the-14.com/the-four-types-of-dementia-most-people-dont-know-exist/

The four types of dementia most people don’t know exist
#Dementia #HealthAwareness #BrainHealth #Alzheimers #Neurology #MedicalEducation #PublicHealth #RareDiseases #MentalHealth #Healthcare #Awareness #Science #Caregiving #Aging
https://the-14.com/the-four-types-of-dementia-most-people-dont-know-exist/

The four types of dementia most people don’t know exist
#Dementia #HealthAwareness #BrainHealth #Alzheimers #Neurology #MedicalEducation #PublicHealth #RareDiseases #MentalHealth #Healthcare #Awareness #Science #Caregiving #Aging
https://the-14.com/the-four-types-of-dementia-most-people-dont-know-exist/

https://www.europesays.com/ch/41723/ Novartis IgAN data in New England Journal of Medicine show Fabhalta® slowed kidney function decline by 49.3% #ClinicalTrials #Novartis #RareDiseases #ReimagineMedicine

I’ll attend the #EuroNDD Workshop in Warsaw in April. Anyone around the Fediverse going there as well? —> let’s connect!

I’m looking forward to present our work at https://www.findme2care.de AND hear about all the other projects.

Also: I’ll be co-hosting an educational session and roundtable discussion titled „Building Patient Registries under the GDPR – The Good, the Bad and the Ugly“ —> there are a few seats left for conference attendees!

#humangenetics #genetics #RareDiseases #RareDisease #ERN #ERNIthaca #patientregistry

I’ll attend the #EuroNDD Workshop in Warsaw in April. Anyone around the Fediverse going there as well? —> let’s connect!

I’m looking forward to present our work at https://www.findme2care.de AND hear about all the other projects.

Also: I’ll be co-hosting an educational session and roundtable discussion titled „Building Patient Registries under the GDPR – The Good, the Bad and the Ugly“ —> there are a few seats left for conference attendees!

#humangenetics #genetics #RareDiseases #RareDisease #ERN #ERNIthaca #patientregistry

I’ll attend the #EuroNDD Workshop in Warsaw in April. Anyone around the Fediverse going there as well? —> let’s connect!

I’m looking forward to present our work at https://www.findme2care.de AND hear about all the other projects.

Also: I’ll be co-hosting an educational session and roundtable discussion titled „Building Patient Registries under the GDPR – The Good, the Bad and the Ugly“ —> there are a few seats left for conference attendees!

#humangenetics #genetics #RareDiseases #RareDisease #ERN #ERNIthaca #patientregistry

I’ll attend the #EuroNDD Workshop in Warsaw in April. Anyone around the Fediverse going there as well? —> let’s connect!

I’m looking forward to present our work at https://www.findme2care.de AND hear about all the other projects.

Also: I’ll be co-hosting an educational session and roundtable discussion titled „Building Patient Registries under the GDPR – The Good, the Bad and the Ugly“ —> there are a few seats left for conference attendees!

#humangenetics #genetics #RareDiseases #RareDisease #ERN #ERNIthaca #patientregistry

I’ll attend the #EuroNDD Workshop in Warsaw in April. Anyone around the Fediverse going there as well? —> let’s connect!

I’m looking forward to present our work at https://www.findme2care.de AND hear about all the other projects.

Also: I’ll be co-hosting an educational session and roundtable discussion titled „Building Patient Registries under the GDPR – The Good, the Bad and the Ugly“ —> there are a few seats left for conference attendees!

#humangenetics #genetics #RareDiseases #RareDisease #ERN #ERNIthaca #patientregistry

https://www.europesays.com/ch/35861/ Roche stops work on experimental SMA drug #MuscularDystrophy #RareDiseases #Roche #ScholarRock #SMAPatients #SpinalMuscularAtrophy

💡 A genuine surprise: The active ingredient in #Viagra, sildenafil, helps treat a rare genetic disorder! This unexpected finding has now been uncovered by researchers at #CharitéBerlin. The drug showed positive effects on the course of the disease in six patients with #Leigh syndrome. More on the promising results:

👉 https://www.charite.de/en/service/press_reports/artikel/detail/active_ingredient_of_viagra_helps_treat_rare_genetic_disease

#medicine #science #research #MedMastodon #RareDiseases