#metachromaticleukodystrophy — Public Fediverse posts
Live and recent posts from across the Fediverse tagged #metachromaticleukodystrophy, aggregated by home.social.
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Lifesaving gene therapy for kids is world’s priciest drug at $4.25M - Enlarge / A mother with her twin 6-year-old boys who have metachromatic... - https://arstechnica.com/?p=2011685 #metachromaticleukodystrophy #raregeneticconditions #drugpricing #genetherapy #science #orchard #health #fda