#sicklecell — Public Fediverse posts
Live and recent posts from across the Fediverse tagged #sicklecell, aggregated by home.social.
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#GeneEditing Therapy Shows Success Against Severe #SickleCell Disease https://newsroom.clevelandclinic.org/2026/04/01/gene-editing-therapy-shows-success-against-severe-sickle-cell-disease
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Orioles blood drive raises awareness for sickle cell disease https://www.rawchili.com/mlb/320069/ #AmericanRedCross #awareness #Baltimore #BaltimoreHospital #BaltimoreHospitals #BaltimoreOrioles #BaltimoreOrioles #Baseball #blood #BloodDonations #BradChambers #condition #decision #Donation #ExecutiveVicePresident #Health #hospital #hospitals #HowToDonateBlood #ManyPeople #maryland #medstar #MedstarHealth #MLB #news #Orioles #OriolesBloodDrive #patient #SickleCell #SickleCellDisease
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Orioles blood drive raises awareness for sickle cell disease https://www.rawchili.com/mlb/320069/ #AmericanRedCross #awareness #Baltimore #BaltimoreHospital #BaltimoreHospitals #BaltimoreOrioles #BaltimoreOrioles #Baseball #blood #BloodDonations #BradChambers #condition #decision #Donation #ExecutiveVicePresident #Health #hospital #hospitals #HowToDonateBlood #ManyPeople #maryland #medstar #MedstarHealth #MLB #news #Orioles #OriolesBloodDrive #patient #SickleCell #SickleCellDisease
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BLOOD DONOR APPEAL: O negative, B negative & black heritage donors needed in #Birmingham
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Many pregnant & breastfeeding women cannot be sure that their needed medications are safe for them – inc. for diseases like #SickleCell - because of exclusion of these groups from clinical trials. 🔗 bit.ly/4e7Pql8
Equity and health: the inclusi... -
https://www.europesays.com/uk/197276/ Sickle Cell Medication Cost Soars – NGO Plea to Nigeria #AffordableMedication #GeneticDisorder #Health #Healthcare #Medication #NGO #Nigeria #PublicHealth #SickleCell #SickleCellDisease #SickleCellMedication #UK #UnitedKingdom #WorldSickleCellDay
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With high quality care, women with #SickleCell disease can have healthy pregnancies and births. They need: 👨🏿⚕️ Access to skilled health workers 🩺 Additional health checks 🤰🏾 Individualized & respectful care 🔬 Research for safe treatments in pregnancy bit.ly/446z3AV
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#SickleCell disease poses life-threatening risks for women & babies. In fact, it leads to a 11X higher risk of maternal death, increased rates of stillbirth, and preterm births. WHO’s new guideline aims to improve pregnancy outcomes for those affected. 🔗 bit.ly/446z3AV
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#SickleCell disease is a group of inherited blood disorders characterized by abnormally shaped red blood cells. These cells can block blood flow, causing - severe anaemia - episodes of severe pain - recurrent infections - emergencies like strokes, sepsis or organ failures bsky.app/profile/who....
RE: https://bsky.app/profile/did:plc:univ47kzorwxjih3lqzrnwmv/post/3lrxexijxos2t -
Today is #SickleCell Awareness Day 🩸 40% more people are living with sickle cell disease today than in 2000. It is a growing health challenge, affecting around 7.7 million people in the world today. Read WHO’s new recommendations on care during pregnancy: bit.ly/446z3AV
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#OnThisDay Birth Anniversary of Blaise Pascal (1623) - French mathematician, physicist, inventor. He made important contributions to the study of fluids, and clarified the concepts of pressure and vacuum.
Today is World #SickleCell Day.
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Discover a 6-step at-home cure for thalassemia, sickle cell anemia & more — based on real success stories using Living Water Therapy—a must-read for patients & caregivers.
#BloodDisorders #Thalassemia #SickleCell #CancerAwareness #LivingWaterTherapy #HealthRevolution
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New York patient receives breakthrough cure for sickle cell disease, 'I’m not in pain anymore’
#genetherapy #health #healthnews #healthcare #LongIsland #Medical #Medicine #NewYork #news #SickleCell
https://theaegisalliance.com/2025/03/14/new-york-patient-receives-breakthrough-cure-for-sickle-cell-disease/?fsp_sid=1170 -
We can cure a genetic disease, not only in mice but in people! New #crispr based #sicklecell therapy fixes stem cells of patients. Now let's make it cheaper. https://www.theguardian.com/society/2025/jan/31/groundbreaking-potential-cure-for-sickle-cell-in-england-approved-for-nhs-use
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"she still struggles with chronic pain in her back and legs caused by decades of tissue and nerve damage from sickle-cell disease."
#sicklecell
#medsky #blacksky #science #complex -
'Last December, the Food and Drug Administration gave approvalto two companies, Bluebird Bio of Somerville, Mass., and Vertex Pharmaceuticals of Boston, to sell the first gene therapies approved for sickle cell disease. After nine months, Kendric remains the first Bluebird patient to progress this far, with at least a few others advancing toward his pace.'
#SickleCell #GeneTherapy
https://www.nytimes.com/2024/09/16/health/sickle-cell-gene-therapy-kendric-cromer.html -
A fantastic story from C&EN about Indian gene therapies for #sicklecell.
In the US, we often think of sickle cell affecting African Americans, but there's a huge crisis in #India, where it's estimated over 1 million(!) people have #SCD.
https://cen.acs.org/pharmaceuticals/gene-therapy/Sickle-cell-disease-India-quest/102/i24
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NEW: #Vertex Pharmaceuticals is suing the gov over blocking access to #fertility preservation services for people getting #Casgevy, the first #CRISPR treatment, which treats #sicklecell & #betathalassemia
Currently, Vertex offering to help patients access these services illegal under anti-kickback laws
via @STAT
https://www.statnews.com/2024/07/15/vertex-casgevy-sickle-cell-infertility-hhs-lawsuit-fertility-preservation/ -
#OnThisDay Birth Anniversary of Blaise Pascal (1623) - French mathematician, physicist, inventor. He made important contributions to the study of fluids, and clarified the concepts of pressure and vacuum.
Today is World #SickleCell Day.
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@jperkel @Nature @heidiledford I did not know about this: "Most of the people with sickle-cell disease in India — a country with one of the highest rates of the condition — live in impoverished communities. "
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@STAT is investigating the denial of reproductive autonomy for people with sickle cell disease.
Their latest article explores "how doctors are pressuring sickle cell patients into unwanted sterilizations."
#SickleCell #Disease #ReproductiveRights #Health #Medicine #Discrimination #BlackMastodon
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First Patient Begins Newly Approved #SickleCell #GeneTherapy https://www.nytimes.com/2024/05/06/health/sickle-cell-cure-first.html
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CRISPR advances Sickle Cell disease treatment - The innovative gene-editing technique, CRISPR, has made a remarkable leap from lab... - https://readwrite.com/crispr-advances-sickle-cell-disease-treatment/ #gene-editingtechniques #medicalbreakthrough #healthcare #sicklecell #startups #news
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Today, two posts in one go, both on #sicklecell disease and #geneediting'; one provides background info, the other homes in on the issue of 'identity' https://blogs.nottingham.ac.uk/makingsciencepublic/2024/01/12/sickle-cell-disease-and-gene-editing/ and https://blogs.nottingham.ac.uk/makingsciencepublic/2024/01/12/sickle-cell-disease-and-identity/
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These #gene therapies are billed as "one time" therapies, basically miracle cures:
Almost 90% of the Zynteglo trial patients were transfusion-independent afterward, for at least 9 years.
The new #sicklecell treatments are similar. https://www.statnews.com/2023/12/08/fda-approves-casgevy-crispr-based-medicine-for-treatment-of-sickle-cell-disease/
#health #healthcare #medicine #scd #crispr #betathalassemia #transplant
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It's been a long time coming...
Today is both Taylor Swift's birthday & the day I get to share the story of Shelby, a 7 (now 8) year old who's in the midst of a year+ "one-time" #genetherapy that will likely cure her #betathalassemia.
Don't miss the Taylor & Emily "The Space Gal" Calandrelli mentions, Shelby's budding #YouTube career, or how Sour Patch Kids are important for gene and #celltherapy:
https://www.statnews.com/2023/12/13/gene-therapy-zynteglo-bluebird-beta-thalassemia/
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In historic decision, FDA approves a CRISPR-based medicine for treatment of sickle cell disease
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"Shortly after the approval their manufacturers announced sticker prices in the millions of dollars: $3.1 million for Lyfgenia, made by Bluebird Bio, and $2.2 million for Casgevy, made by Vertex Pharmaceuticals."
#SickleCell #GeneTherapyhttps://www.nytimes.com/2023/12/08/health/casgevy-lyfgenia-sickle-cell-africa.html
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From Alex Dainis Ph.D. (Wish she would post on Mastodon, she's so good ☹️) about the "very first approved CRISPR gene editing therapy in the US. Breaking genetics news, so I had to talk about it. Tell me what you want to know!"
https://x.com/AlexDainis/status/1733321710991257796?s=20
#genetherapy #crispr #geneediting #genetics #sicklecell #casgevy
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Sickle cell disease predominantly affects those of #African, #Mediterranean, #Hispanic, #MiddleEastern, and #Asian #descent, linked to the #sicklecell #trait's #protective #effect against #malaria in these #regions. Nonetheless, it can occur in people of any #ethnicity.
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#US #approves first #geneediting #treatment, #Casgevy, for #SickleCellDisease.
#SickleCell, an inherited #blood #disorder, causes #redbloodcells to become misshapen half moons that get stuck inside #blood #vessels, #restricting #bloodflow and causing what are known as #paincrises.
#Women #Transgender #LGBTQ #LGBTQIA #Health #Healthcare #Progress #BlackMastodon
https://www.cnbc.com/2023/12/08/casgevy-first-crispr-gene-editing-treatment-approved-in-us.html
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#US #approves first #geneediting #treatment, #Casgevy, for #SickleCellDisease.
#SickleCell, an inherited #blood #disorder, causes #redbloodcells to become misshapen half moons that get stuck inside #blood #vessels, #restricting #bloodflow and causing what are known as #paincrises.
#Women #Transgender #LGBTQ #LGBTQIA #Health #Healthcare #Progress #BlackMastodon
https://www.cnbc.com/2023/12/08/casgevy-first-crispr-gene-editing-treatment-approved-in-us.html
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#US #approves first #geneediting #treatment, #Casgevy, for #SickleCellDisease.
#SickleCell, an inherited #blood #disorder, causes #redbloodcells to become misshapen half moons that get stuck inside #blood #vessels, #restricting #bloodflow and causing what are known as #paincrises.
#Women #Transgender #LGBTQ #LGBTQIA #Health #Healthcare #Progress #BlackMastodon
https://www.cnbc.com/2023/12/08/casgevy-first-crispr-gene-editing-treatment-approved-in-us.html
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#US #approves first #geneediting #treatment, #Casgevy, for #SickleCellDisease.
#SickleCell, an inherited #blood #disorder, causes #redbloodcells to become misshapen half moons that get stuck inside #blood #vessels, #restricting #bloodflow and causing what are known as #paincrises.
#Women #Transgender #LGBTQ #LGBTQIA #Health #Healthcare #Progress #BlackMastodon
https://www.cnbc.com/2023/12/08/casgevy-first-crispr-gene-editing-treatment-approved-in-us.html
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#US #approves first #geneediting #treatment, #Casgevy, for #SickleCellDisease.
#SickleCell, an inherited #blood #disorder, causes #redbloodcells to become misshapen half moons that get stuck inside #blood #vessels, #restricting #bloodflow and causing what are known as #paincrises.
#Women #Transgender #LGBTQ #LGBTQIA #Health #Healthcare #Progress #BlackMastodon
https://www.cnbc.com/2023/12/08/casgevy-first-crispr-gene-editing-treatment-approved-in-us.html
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Answers to questions about the first CRISPR-based medicine:
https://www.statnews.com/2023/11/16/crispr-vertex-sickle-cell-beta-thalassemia-casgevy-approval/#health #healthcare #medicine #biotech #pharma #crispr #genetherapy #geneediting #scd #SickleCell #casgevy #lyfgenia
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Most of the sickle cell community is African-American, and with that comes a lot of medical mistrust, especially for a brand-new technology.
From a sickle cell patient herself:
https://www.statnews.com/2023/12/08/casgevy-lyfgenia-vertex-bluebird-sickle-cell-gene-therapy-approval-patients/#health #healthcare #medicine #biotech #pharma #crispr #genetherapy #geneediting #scd #SickleCell #casgevy #lyfgenia #healthequity
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Adam Feuerstein spoke with #CRISPR Therapeutics CEO Sam Kulkarni on the approval and future of CRISPR-based medicines:
https://www.statnews.com/2023/12/08/crispr-therapeutics-ceo-samarth-kulkarni-interview/
#health #healthcare #medicine #biotech #pharma #crispr #genetherapy #geneediting #scd #SickleCell #casgevy -
Don't miss the rest of STAT's coverage of this historic moment:
https://www.statnews.com/2023/12/08/fda-approves-casgevy-crispr-based-medicine-for-treatment-of-sickle-cell-disease/#health #healthcare #medicine #biotech #pharma #crispr #genetherapy #geneediting #scd #SickleCell #casgevy #lyfgenia #zynteglo
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Today the FDA approved 2 gene therapies to treat sickle cell disease, including the first CRISPR-based therapy.
Bluebird Bio, who has the ~$1M more expensive and not-CRISPR therapy, has a single card left to play in this competition: It's been conducting a year-long dress rehearsal for this moment
#health #healthcare #medicine #biotech #pharma #crispr #genetherapy #geneediting #scd #SickleCell #casgevy #lyfgenia #zynteglo
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The Food and Drug Administration on Friday approved a powerful 👉treatment for 🔸sickle cell disease🔸, a devastating illness that affects more than 100,000 Americans, the majority of whom are Black.
The therapy, called "Casgevy", from Vertex Pharmaceuticals and CRISPR Therapeutics, is the ⚠️first medicine to be approved in the United States that uses the gene-editing tool 🔹CRISPR🔹, which won its inventors the Nobel Prize in chemistry in 2020.The approval marks the first of two potential breakthroughs for the inherited blood disorder.
The FDA on Friday also approved a 👉second treatment for sickle cell disease, called "Lyfgenia", a gene therapy from drugmaker Bluebird Bio.
Both treatments work by genetically modifying a patient’s own stem cells.Until now, the only known cure for sickle cell disease was a bone marrow transplant from a donor, which carries the risk of rejection by the immune system, in addition to the difficult process of finding a matching donor.
#casgevy #lyfgenia #crisper #Sicklecelldisease #sicklecell
https://www.nbcnews.com/health/health-news/fda-approves-cure-sickle-cell-disease-first-treatment-use-gene-editing-rcna127979 -
A world first, a marker of progress
Gene therapy now approved in the UK
No more suffering
For sickle cell bearing
A medical breakthrough, of such success -
A group of academic and industry researchers exhibited in lab cells and mice a more direct delivery technique that could make gene therapies more accessible and inexpensive.
https://sciencebusiness.technewslit.com/?p=45041
#News #Press #Science #Business #Biotechnology #Genetics #GeneTherapy #LipidNanoparticles #mRNA #SickleCell #StemCells #Preclinical #BoneMarrow
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Hot off the presses: our 2023 overview of #CRISPR in clinical trials! Reader-friendly. Read here & share: http://ow.ly/wj4W50NlJcm
#GeneticDisease #genetics #genomics #RareDisease #cancer #SickleCell #HIV #UTI #DMD #leukemia #lymphoma #diabetes #research #innovation
