#rnasplicing — Public Fediverse posts
Live and recent posts from across the Fediverse tagged #rnasplicing, aggregated by home.social.
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PepGen Announces Topline Results from Lowest Dose (5 mg/kg) MAD Cohort in the Ongoing Phase 2 FREEDOM2 Study Demonstrating Favorable Safety, Splicing and vHOT Data
– PGN-EDODM1 was generally well-tolerated with all adverse events mild or moderate and no serious adverse events reported…
#NewsBeep #News #Medication #CA #Canada #clinicalresults #FREEDOM2 #Health #neurologicaldiseases #oligonucleotide #patients #PepGen #RNAsplicing #TheCompany
https://www.newsbeep.com/ca/575804/ -
https://www.europesays.com/ie/?p=415382 PepGen Announces Topline Results from Lowest Dose (5 mg/kg) MAD Cohort in the Ongoing Phase 2 FREEDOM2 Study Demonstrating Favorable Safety, Splicing and vHOT Data #ClinicalResults #Éire #FREEDOM2 #Health #IE #Ireland #Medication #NeurologicalDiseases #Oligonucleotide #patients #PepGen #RNASplicing #TheCompany
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PepGen Announces Topline Results from Lowest Dose (5 mg/kg) MAD Cohort in the Ongoing Phase 2 FREEDOM2 Study Demonstrating Favorable Safety, Splicing and vHOT Data
– PGN-EDODM1 was generally well-tolerated with all adverse events mild or moderate and no serious adverse events reported…
#NewsBeep #News #Medication #clinicalresults #FREEDOM2 #Health #neurologicaldiseases #oligonucleotide #Patients #PepGen #RNAsplicing #TheCompany #UK #UnitedKingdom
https://www.newsbeep.com/uk/507180/ -
This study shows that #RNAsplicing is widely dysregulated when #FMRP is lost; this involves multiple splicing factors, including MBNL1. In FMRP-depleted cells, Mbnl1 RNA is misspliced, mislocalizing #MBNL1, and in turn messing up further RNAs #PLOSBiology https://plos.io/3R6E9GN