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#orphandesignation — Public Fediverse posts

Live and recent posts from across the Fediverse tagged #orphandesignation, aggregated by home.social.

  1. France @[email protected] ·

    Press Release: Sanofi’s venglustat accepted for priority review in the US to treat type 3 Gaucher disease

    Sanofi Winthrop Industrie Sanofi’s venglustat accepted for priority review in the US to treat type 3 Gaucher disease…
    #France #FR #Europe #EU #Sanofi #bloodbrainbarrier #ERT #Fabrydisease #Gaucherdisease #neurologicalmanifestations #orphandesignation #pediatricpatients #potential
    europesays.com/france/26133/

    #potential #pediatricpatients #orphandesignation #neurologicalmanifestations #gaucherdisease #fabrydisease
  2. France @[email protected] ·

    Press Release: Sanofi’s venglustat accepted for priority review in the US to treat type 3 Gaucher disease

    Sanofi Winthrop Industrie Sanofi’s venglustat accepted for priority review in the US to treat type 3 Gaucher disease…
    #France #FR #Europe #EU #Sanofi #bloodbrainbarrier #ERT #Fabrydisease #Gaucherdisease #neurologicalmanifestations #orphandesignation #pediatricpatients #potential
    europesays.com/france/26078/

    #potential #pediatricpatients #orphandesignation #neurologicalmanifestations #gaucherdisease #fabrydisease