#casgevy — Public Fediverse posts
Live and recent posts from across the Fediverse tagged #casgevy, aggregated by home.social.
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https://www.europesays.com/ie/608170/ 7 life-saving medical innovations that could redefine healthcare #ArtificialIntelligence #BiomedicalEngineering #Biotechnology #Casgevy #CRISPR #DrugDiscovery #Éire #FutureMedicine #Health #HealthCare #Healthcare #HealthcareInnovation #IE #Ireland #MedicalResearch #MedicalScience #PersonalizedCancerVaccines #RegenerativeMedicine #StemCells #Type1Diabetes #Xenotransplantation
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Vertex (VRTX) Wins FDA Expansion For CASGEVY And Advances ALYFTREK In Canada
Find winning stocks in any market cycle. Join 7 million investors using Simply Wall St’s investing ideas for…
#Canada #ALYFTREK #betathalassemia #CASGEVY #cysticfibrosis #sicklecelldisease #VertexPharmaceuticals
https://www.europesays.com/canada/126364/ -
🔥 TRENDING
📢 Crispr: Casgevy bringt 43 Millionen Dollar Umsatz - Börse Express
#Crispr #Casgevy #Millionen #Dollar #GlobalFeed #News #DE
*Automatisch gepostet von Global Feed Bot*
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Vertex’s Germany CASGEVY Deal Highlights Growing Non CF Growth Story
Find winning stocks in any market cycle. Join 7 million investors using Simply Wall St’s investing ideas for…
#Germany #DE #Europe #EU #Europa #CASGEVY #cysticfibrosis #reimbursement #stocktrades #VertexPharmaceuticals
https://www.europesays.com/germany/12629/ -
https://www.europesays.com/uk/502523/ Reporter’s Notebook: The Overdue Breakout for Gene Therapy and Gene Editing #casgevy #CellTherapy #crispr #GeneTherapy(therapeutics) #Genetics #glioblastoma #IssueNo.03 #May152014 #MetabolicDisorders #News&Features #oncology #PrecisionMedicine #PrimeMedicine #Science #topics #TranslationalResearch #trogenix #UK #UnitedKingdom #VertexPharmaceuticals #Volume01
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Reporter’s Notebook: The Overdue Breakout for Gene Therapy and Gene Editing
As gene editing enters a new era, leaders discuss Baby KJ’s implications for families, sc…
#NewsBeep #News #Genetics #AU #Australia #casgevy #Celltherapy #CRISPR #genetherapy(therapeutics) #glioblastoma #issueno.03 #may152014 #MetabolicDisorders #news&features #oncology #Precisionmedicine #primemedicine #Science #topics #translationalresearch #trogenix #VertexPharmaceuticals #volume01
https://www.newsbeep.com/au/216143/ -
NEW: #Vertex Pharmaceuticals is suing the gov over blocking access to #fertility preservation services for people getting #Casgevy, the first #CRISPR treatment, which treats #sicklecell & #betathalassemia
Currently, Vertex offering to help patients access these services illegal under anti-kickback laws
via @STAT
https://www.statnews.com/2024/07/15/vertex-casgevy-sickle-cell-infertility-hhs-lawsuit-fertility-preservation/ -
NEW: #Vertex Pharmaceuticals is suing the gov over blocking access to #fertility preservation services for people getting #Casgevy, the first #CRISPR treatment, which treats #sicklecell & #betathalassemia
Currently, Vertex offering to help patients access these services illegal under anti-kickback laws
via @STAT
https://www.statnews.com/2024/07/15/vertex-casgevy-sickle-cell-infertility-hhs-lawsuit-fertility-preservation/ -
NEW: #Vertex Pharmaceuticals is suing the gov over blocking access to #fertility preservation services for people getting #Casgevy, the first #CRISPR treatment, which treats #sicklecell & #betathalassemia
Currently, Vertex offering to help patients access these services illegal under anti-kickback laws
via @STAT
https://www.statnews.com/2024/07/15/vertex-casgevy-sickle-cell-infertility-hhs-lawsuit-fertility-preservation/ -
NEW: #Vertex Pharmaceuticals is suing the gov over blocking access to #fertility preservation services for people getting #Casgevy, the first #CRISPR treatment, which treats #sicklecell & #betathalassemia
Currently, Vertex offering to help patients access these services illegal under anti-kickback laws
via @STAT
https://www.statnews.com/2024/07/15/vertex-casgevy-sickle-cell-infertility-hhs-lawsuit-fertility-preservation/ -
¿Quieres conocer cómo hemos llegado a aprobar #Casgevy, la primera terapia #CRISPR para tratar enfermedades, desde una investigación básica inicial en arqueas de las salinas de Santa Pola?
Te lo cuento a traves de 10 hitos científicos ocurridos durante 30 años en mi blog #gen_ética en @Naukas_com
https://montoliu.naukas.com/2023/12/17/desde-las-salinas-de-santa-pola-a-casgevy/ -
¿Quieres conocer cómo hemos llegado a aprobar #Casgevy, la primera terapia #CRISPR para tratar enfermedades, desde una investigación básica inicial en arqueas de las salinas de Santa Pola?
Te lo cuento a traves de 10 hitos científicos ocurridos durante 30 años en mi blog #gen_ética en @Naukas_com
https://montoliu.naukas.com/2023/12/17/desde-las-salinas-de-santa-pola-a-casgevy/ -
¿Quieres conocer cómo hemos llegado a aprobar #Casgevy, la primera terapia #CRISPR para tratar enfermedades, desde una investigación básica inicial en arqueas de las salinas de Santa Pola?
Te lo cuento a traves de 10 hitos científicos ocurridos durante 30 años en mi blog #gen_ética en @Naukas_com
https://montoliu.naukas.com/2023/12/17/desde-las-salinas-de-santa-pola-a-casgevy/ -
¿Quieres conocer cómo hemos llegado a aprobar #Casgevy, la primera terapia #CRISPR para tratar enfermedades, desde una investigación básica inicial en arqueas de las salinas de Santa Pola?
Te lo cuento a traves de 10 hitos científicos ocurridos durante 30 años en mi blog #gen_ética en @Naukas_com
https://montoliu.naukas.com/2023/12/17/desde-las-salinas-de-santa-pola-a-casgevy/ -
Estupendo artículo de @manuelansede hoy en @materia_ciencia @el_pais resumiendo la revolución #CRISPR desde los inicios con Francis Mojica en las salinas de Santa Pola hasta la aprobación de la primera terapia #Casgevy aprobada ya en RU, EEUU y pronto UE.
https://elpais.com/ciencia/2023-12-17/nace-la-medicina-crispr-con-la-promesa-de-salvar-millones-de-vidas.html -
Estupendo artículo de @manuelansede hoy en @materia_ciencia @el_pais resumiendo la revolución #CRISPR desde los inicios con Francis Mojica en las salinas de Santa Pola hasta la aprobación de la primera terapia #Casgevy aprobada ya en RU, EEUU y pronto UE.
https://elpais.com/ciencia/2023-12-17/nace-la-medicina-crispr-con-la-promesa-de-salvar-millones-de-vidas.html -
Estupendo artículo de @manuelansede hoy en @materia_ciencia @el_pais resumiendo la revolución #CRISPR desde los inicios con Francis Mojica en las salinas de Santa Pola hasta la aprobación de la primera terapia #Casgevy aprobada ya en RU, EEUU y pronto UE.
https://elpais.com/ciencia/2023-12-17/nace-la-medicina-crispr-con-la-promesa-de-salvar-millones-de-vidas.html -
Hoy la Agencia Europea del Medicamento (EMA) ha recomendado la autorización de #Casgevy la primera terapia #CRISPR para tratar anemia falciforme y beta talasemia. He publicado una opinión en Science Media Centre ES
https://sciencemediacentre.es/reaccion-la-ema-da-luz-verde-al-primer-medicamento-en-la-ue-que-utiliza-la-edicion-genetica-de -
Hoy la Agencia Europea del Medicamento (EMA) ha recomendado la autorización de #Casgevy la primera terapia #CRISPR para tratar anemia falciforme y beta talasemia. He publicado una opinión en Science Media Centre ES
https://sciencemediacentre.es/reaccion-la-ema-da-luz-verde-al-primer-medicamento-en-la-ue-que-utiliza-la-edicion-genetica-de -
Hoy la Agencia Europea del Medicamento (EMA) ha recomendado la autorización de #Casgevy la primera terapia #CRISPR para tratar anemia falciforme y beta talasemia. He publicado una opinión en Science Media Centre ES
https://sciencemediacentre.es/reaccion-la-ema-da-luz-verde-al-primer-medicamento-en-la-ue-que-utiliza-la-edicion-genetica-de -
Hoy la Agencia Europea del Medicamento (EMA) ha recomendado la autorización de #Casgevy la primera terapia #CRISPR para tratar anemia falciforme y beta talasemia. He publicado una opinión en Science Media Centre ES
https://sciencemediacentre.es/reaccion-la-ema-da-luz-verde-al-primer-medicamento-en-la-ue-que-utiliza-la-edicion-genetica-de -
I thought that the fantastical price tag might be keeping some patients from getting #Zynteglo
Turns out, that doesn't seem to be the case (yet), as I detail in a sister piece about Bluebird and the #insurance logistics behind these therapies:
#health #healthcare #scd #crispr #betathalassemia #transplant #lyfgenia #casgevy #healthinsurance #pharma #bigpharma #biotech
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I thought that the fantastical price tag might be keeping some patients from getting #Zynteglo
Turns out, that doesn't seem to be the case (yet), as I detail in a sister piece about Bluebird and the #insurance logistics behind these therapies:
#health #healthcare #scd #crispr #betathalassemia #transplant #lyfgenia #casgevy #healthinsurance #pharma #bigpharma #biotech
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I thought that the fantastical price tag might be keeping some patients from getting #Zynteglo
Turns out, that doesn't seem to be the case (yet), as I detail in a sister piece about Bluebird and the #insurance logistics behind these therapies:
#health #healthcare #scd #crispr #betathalassemia #transplant #lyfgenia #casgevy #healthinsurance #pharma #bigpharma #biotech
-
I thought that the fantastical price tag might be keeping some patients from getting #Zynteglo
Turns out, that doesn't seem to be the case (yet), as I detail in a sister piece about Bluebird and the #insurance logistics behind these therapies:
#health #healthcare #scd #crispr #betathalassemia #transplant #lyfgenia #casgevy #healthinsurance #pharma #bigpharma #biotech
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Confirmado. El precio de adquisición de #CASGEVY la nueva terapia #CRISPR producida por @vertexpharma (junto a @crisprtx) para tratar la anemia falciforme y la beta talasemia en EE.UU. en pacientes de 12 o más años será de 2,2 millones de dólares (2,2M$)
https://www.sec.gov/ix?doc=/Archives/edgar/data/0000875320/000087532023000054/vrtx-20231208.htm -
Confirmado. El precio de adquisición de #CASGEVY la nueva terapia #CRISPR producida por @vertexpharma (junto a @crisprtx) para tratar la anemia falciforme y la beta talasemia en EE.UU. en pacientes de 12 o más años será de 2,2 millones de dólares (2,2M$)
https://www.sec.gov/ix?doc=/Archives/edgar/data/0000875320/000087532023000054/vrtx-20231208.htm -
Confirmado. El precio de adquisición de #CASGEVY la nueva terapia #CRISPR producida por @vertexpharma (junto a @crisprtx) para tratar la anemia falciforme y la beta talasemia en EE.UU. en pacientes de 12 o más años será de 2,2 millones de dólares (2,2M$)
https://www.sec.gov/ix?doc=/Archives/edgar/data/0000875320/000087532023000054/vrtx-20231208.htm -
Confirmado. El precio de adquisición de #CASGEVY la nueva terapia #CRISPR producida por @vertexpharma (junto a @crisprtx) para tratar la anemia falciforme y la beta talasemia en EE.UU. en pacientes de 12 o más años será de 2,2 millones de dólares (2,2M$)
https://www.sec.gov/ix?doc=/Archives/edgar/data/0000875320/000087532023000054/vrtx-20231208.htm -
From Alex Dainis Ph.D. (Wish she would post on Mastodon, she's so good ☹️) about the "very first approved CRISPR gene editing therapy in the US. Breaking genetics news, so I had to talk about it. Tell me what you want to know!"
https://x.com/AlexDainis/status/1733321710991257796?s=20
#genetherapy #crispr #geneediting #genetics #sicklecell #casgevy
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From Alex Dainis Ph.D. (Wish she would post on Mastodon, she's so good ☹️) about the "very first approved CRISPR gene editing therapy in the US. Breaking genetics news, so I had to talk about it. Tell me what you want to know!"
https://x.com/AlexDainis/status/1733321710991257796?s=20
#genetherapy #crispr #geneediting #genetics #sicklecell #casgevy
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From Alex Dainis Ph.D. (Wish she would post on Mastodon, she's so good ☹️) about the "very first approved CRISPR gene editing therapy in the US. Breaking genetics news, so I had to talk about it. Tell me what you want to know!"
https://x.com/AlexDainis/status/1733321710991257796?s=20
#genetherapy #crispr #geneediting #genetics #sicklecell #casgevy
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From Alex Dainis Ph.D. (Wish she would post on Mastodon, she's so good ☹️) about the "very first approved CRISPR gene editing therapy in the US. Breaking genetics news, so I had to talk about it. Tell me what you want to know!"
https://x.com/AlexDainis/status/1733321710991257796?s=20
#genetherapy #crispr #geneediting #genetics #sicklecell #casgevy
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#US #approves first #geneediting #treatment, #Casgevy, for #SickleCellDisease.
#SickleCell, an inherited #blood #disorder, causes #redbloodcells to become misshapen half moons that get stuck inside #blood #vessels, #restricting #bloodflow and causing what are known as #paincrises.
#Women #Transgender #LGBTQ #LGBTQIA #Health #Healthcare #Progress #BlackMastodon
https://www.cnbc.com/2023/12/08/casgevy-first-crispr-gene-editing-treatment-approved-in-us.html
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#US #approves first #geneediting #treatment, #Casgevy, for #SickleCellDisease.
#SickleCell, an inherited #blood #disorder, causes #redbloodcells to become misshapen half moons that get stuck inside #blood #vessels, #restricting #bloodflow and causing what are known as #paincrises.
#Women #Transgender #LGBTQ #LGBTQIA #Health #Healthcare #Progress #BlackMastodon
https://www.cnbc.com/2023/12/08/casgevy-first-crispr-gene-editing-treatment-approved-in-us.html
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#US #approves first #geneediting #treatment, #Casgevy, for #SickleCellDisease.
#SickleCell, an inherited #blood #disorder, causes #redbloodcells to become misshapen half moons that get stuck inside #blood #vessels, #restricting #bloodflow and causing what are known as #paincrises.
#Women #Transgender #LGBTQ #LGBTQIA #Health #Healthcare #Progress #BlackMastodon
https://www.cnbc.com/2023/12/08/casgevy-first-crispr-gene-editing-treatment-approved-in-us.html
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#US #approves first #geneediting #treatment, #Casgevy, for #SickleCellDisease.
#SickleCell, an inherited #blood #disorder, causes #redbloodcells to become misshapen half moons that get stuck inside #blood #vessels, #restricting #bloodflow and causing what are known as #paincrises.
#Women #Transgender #LGBTQ #LGBTQIA #Health #Healthcare #Progress #BlackMastodon
https://www.cnbc.com/2023/12/08/casgevy-first-crispr-gene-editing-treatment-approved-in-us.html
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Answers to questions about the first CRISPR-based medicine:
https://www.statnews.com/2023/11/16/crispr-vertex-sickle-cell-beta-thalassemia-casgevy-approval/#health #healthcare #medicine #biotech #pharma #crispr #genetherapy #geneediting #scd #SickleCell #casgevy #lyfgenia
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Answers to questions about the first CRISPR-based medicine:
https://www.statnews.com/2023/11/16/crispr-vertex-sickle-cell-beta-thalassemia-casgevy-approval/#health #healthcare #medicine #biotech #pharma #crispr #genetherapy #geneediting #scd #SickleCell #casgevy #lyfgenia
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Answers to questions about the first CRISPR-based medicine:
https://www.statnews.com/2023/11/16/crispr-vertex-sickle-cell-beta-thalassemia-casgevy-approval/#health #healthcare #medicine #biotech #pharma #crispr #genetherapy #geneediting #scd #SickleCell #casgevy #lyfgenia
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Answers to questions about the first CRISPR-based medicine:
https://www.statnews.com/2023/11/16/crispr-vertex-sickle-cell-beta-thalassemia-casgevy-approval/#health #healthcare #medicine #biotech #pharma #crispr #genetherapy #geneediting #scd #SickleCell #casgevy #lyfgenia
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Most of the sickle cell community is African-American, and with that comes a lot of medical mistrust, especially for a brand-new technology.
From a sickle cell patient herself:
https://www.statnews.com/2023/12/08/casgevy-lyfgenia-vertex-bluebird-sickle-cell-gene-therapy-approval-patients/#health #healthcare #medicine #biotech #pharma #crispr #genetherapy #geneediting #scd #SickleCell #casgevy #lyfgenia #healthequity
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Most of the sickle cell community is African-American, and with that comes a lot of medical mistrust, especially for a brand-new technology.
From a sickle cell patient herself:
https://www.statnews.com/2023/12/08/casgevy-lyfgenia-vertex-bluebird-sickle-cell-gene-therapy-approval-patients/#health #healthcare #medicine #biotech #pharma #crispr #genetherapy #geneediting #scd #SickleCell #casgevy #lyfgenia #healthequity
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Most of the sickle cell community is African-American, and with that comes a lot of medical mistrust, especially for a brand-new technology.
From a sickle cell patient herself:
https://www.statnews.com/2023/12/08/casgevy-lyfgenia-vertex-bluebird-sickle-cell-gene-therapy-approval-patients/#health #healthcare #medicine #biotech #pharma #crispr #genetherapy #geneediting #scd #SickleCell #casgevy #lyfgenia #healthequity
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Most of the sickle cell community is African-American, and with that comes a lot of medical mistrust, especially for a brand-new technology.
From a sickle cell patient herself:
https://www.statnews.com/2023/12/08/casgevy-lyfgenia-vertex-bluebird-sickle-cell-gene-therapy-approval-patients/#health #healthcare #medicine #biotech #pharma #crispr #genetherapy #geneediting #scd #SickleCell #casgevy #lyfgenia #healthequity
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Adam Feuerstein spoke with #CRISPR Therapeutics CEO Sam Kulkarni on the approval and future of CRISPR-based medicines:
https://www.statnews.com/2023/12/08/crispr-therapeutics-ceo-samarth-kulkarni-interview/
#health #healthcare #medicine #biotech #pharma #crispr #genetherapy #geneediting #scd #SickleCell #casgevy -
Adam Feuerstein spoke with #CRISPR Therapeutics CEO Sam Kulkarni on the approval and future of CRISPR-based medicines:
https://www.statnews.com/2023/12/08/crispr-therapeutics-ceo-samarth-kulkarni-interview/
#health #healthcare #medicine #biotech #pharma #crispr #genetherapy #geneediting #scd #SickleCell #casgevy -
Adam Feuerstein spoke with #CRISPR Therapeutics CEO Sam Kulkarni on the approval and future of CRISPR-based medicines:
https://www.statnews.com/2023/12/08/crispr-therapeutics-ceo-samarth-kulkarni-interview/
#health #healthcare #medicine #biotech #pharma #crispr #genetherapy #geneediting #scd #SickleCell #casgevy -
Adam Feuerstein spoke with #CRISPR Therapeutics CEO Sam Kulkarni on the approval and future of CRISPR-based medicines:
https://www.statnews.com/2023/12/08/crispr-therapeutics-ceo-samarth-kulkarni-interview/
#health #healthcare #medicine #biotech #pharma #crispr #genetherapy #geneediting #scd #SickleCell #casgevy -
Don't miss the rest of STAT's coverage of this historic moment:
https://www.statnews.com/2023/12/08/fda-approves-casgevy-crispr-based-medicine-for-treatment-of-sickle-cell-disease/#health #healthcare #medicine #biotech #pharma #crispr #genetherapy #geneediting #scd #SickleCell #casgevy #lyfgenia #zynteglo
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Don't miss the rest of STAT's coverage of this historic moment:
https://www.statnews.com/2023/12/08/fda-approves-casgevy-crispr-based-medicine-for-treatment-of-sickle-cell-disease/#health #healthcare #medicine #biotech #pharma #crispr #genetherapy #geneediting #scd #SickleCell #casgevy #lyfgenia #zynteglo
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Don't miss the rest of STAT's coverage of this historic moment:
https://www.statnews.com/2023/12/08/fda-approves-casgevy-crispr-based-medicine-for-treatment-of-sickle-cell-disease/#health #healthcare #medicine #biotech #pharma #crispr #genetherapy #geneediting #scd #SickleCell #casgevy #lyfgenia #zynteglo
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Don't miss the rest of STAT's coverage of this historic moment:
https://www.statnews.com/2023/12/08/fda-approves-casgevy-crispr-based-medicine-for-treatment-of-sickle-cell-disease/#health #healthcare #medicine #biotech #pharma #crispr #genetherapy #geneediting #scd #SickleCell #casgevy #lyfgenia #zynteglo
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Today the FDA approved 2 gene therapies to treat sickle cell disease, including the first CRISPR-based therapy.
Bluebird Bio, who has the ~$1M more expensive and not-CRISPR therapy, has a single card left to play in this competition: It's been conducting a year-long dress rehearsal for this moment
#health #healthcare #medicine #biotech #pharma #crispr #genetherapy #geneediting #scd #SickleCell #casgevy #lyfgenia #zynteglo
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Today the FDA approved 2 gene therapies to treat sickle cell disease, including the first CRISPR-based therapy.
Bluebird Bio, who has the ~$1M more expensive and not-CRISPR therapy, has a single card left to play in this competition: It's been conducting a year-long dress rehearsal for this moment
#health #healthcare #medicine #biotech #pharma #crispr #genetherapy #geneediting #scd #SickleCell #casgevy #lyfgenia #zynteglo
-
Today the FDA approved 2 gene therapies to treat sickle cell disease, including the first CRISPR-based therapy.
Bluebird Bio, who has the ~$1M more expensive and not-CRISPR therapy, has a single card left to play in this competition: It's been conducting a year-long dress rehearsal for this moment
#health #healthcare #medicine #biotech #pharma #crispr #genetherapy #geneediting #scd #SickleCell #casgevy #lyfgenia #zynteglo
-
Today the FDA approved 2 gene therapies to treat sickle cell disease, including the first CRISPR-based therapy.
Bluebird Bio, who has the ~$1M more expensive and not-CRISPR therapy, has a single card left to play in this competition: It's been conducting a year-long dress rehearsal for this moment
#health #healthcare #medicine #biotech #pharma #crispr #genetherapy #geneediting #scd #SickleCell #casgevy #lyfgenia #zynteglo
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The Food and Drug Administration on Friday approved a powerful 👉treatment for 🔸sickle cell disease🔸, a devastating illness that affects more than 100,000 Americans, the majority of whom are Black.
The therapy, called "Casgevy", from Vertex Pharmaceuticals and CRISPR Therapeutics, is the ⚠️first medicine to be approved in the United States that uses the gene-editing tool 🔹CRISPR🔹, which won its inventors the Nobel Prize in chemistry in 2020.The approval marks the first of two potential breakthroughs for the inherited blood disorder.
The FDA on Friday also approved a 👉second treatment for sickle cell disease, called "Lyfgenia", a gene therapy from drugmaker Bluebird Bio.
Both treatments work by genetically modifying a patient’s own stem cells.Until now, the only known cure for sickle cell disease was a bone marrow transplant from a donor, which carries the risk of rejection by the immune system, in addition to the difficult process of finding a matching donor.
#casgevy #lyfgenia #crisper #Sicklecelldisease #sicklecell
https://www.nbcnews.com/health/health-news/fda-approves-cure-sickle-cell-disease-first-treatment-use-gene-editing-rcna127979 -
The Food and Drug Administration on Friday approved a powerful 👉treatment for 🔸sickle cell disease🔸, a devastating illness that affects more than 100,000 Americans, the majority of whom are Black.
The therapy, called "Casgevy", from Vertex Pharmaceuticals and CRISPR Therapeutics, is the ⚠️first medicine to be approved in the United States that uses the gene-editing tool 🔹CRISPR🔹, which won its inventors the Nobel Prize in chemistry in 2020.The approval marks the first of two potential breakthroughs for the inherited blood disorder.
The FDA on Friday also approved a 👉second treatment for sickle cell disease, called "Lyfgenia", a gene therapy from drugmaker Bluebird Bio.
Both treatments work by genetically modifying a patient’s own stem cells.Until now, the only known cure for sickle cell disease was a bone marrow transplant from a donor, which carries the risk of rejection by the immune system, in addition to the difficult process of finding a matching donor.
#casgevy #lyfgenia #crisper #Sicklecelldisease #sicklecell
https://www.nbcnews.com/health/health-news/fda-approves-cure-sickle-cell-disease-first-treatment-use-gene-editing-rcna127979 -
The Food and Drug Administration on Friday approved a powerful 👉treatment for 🔸sickle cell disease🔸, a devastating illness that affects more than 100,000 Americans, the majority of whom are Black.
The therapy, called "Casgevy", from Vertex Pharmaceuticals and CRISPR Therapeutics, is the ⚠️first medicine to be approved in the United States that uses the gene-editing tool 🔹CRISPR🔹, which won its inventors the Nobel Prize in chemistry in 2020.The approval marks the first of two potential breakthroughs for the inherited blood disorder.
The FDA on Friday also approved a 👉second treatment for sickle cell disease, called "Lyfgenia", a gene therapy from drugmaker Bluebird Bio.
Both treatments work by genetically modifying a patient’s own stem cells.Until now, the only known cure for sickle cell disease was a bone marrow transplant from a donor, which carries the risk of rejection by the immune system, in addition to the difficult process of finding a matching donor.
#casgevy #lyfgenia #crisper #Sicklecelldisease #sicklecell
https://www.nbcnews.com/health/health-news/fda-approves-cure-sickle-cell-disease-first-treatment-use-gene-editing-rcna127979