#antisense — Public Fediverse posts

`These data set the stage for a potential therapeutic strategy using antisense oligonucleotides to promote isoform switching in patients with RTT who carry partially functioning alleles of MECP2.`

https://www.science.org/doi/10.1126/scitranslmed.adq4529

#Rett #RettSyndrome #geneTherapy #antisense

`These data set the stage for a potential therapeutic strategy using antisense oligonucleotides to promote isoform switching in patients with RTT who carry partially functioning alleles of MECP2.`

https://www.science.org/doi/10.1126/scitranslmed.adq4529

#Rett #RettSyndrome #geneTherapy #antisense

`These data set the stage for a potential therapeutic strategy using antisense oligonucleotides to promote isoform switching in patients with RTT who carry partially functioning alleles of MECP2.`

https://www.science.org/doi/10.1126/scitranslmed.adq4529

#Rett #RettSyndrome #geneTherapy #antisense

`These data set the stage for a potential therapeutic strategy using antisense oligonucleotides to promote isoform switching in patients with RTT who carry partially functioning alleles of MECP2.`

https://www.science.org/doi/10.1126/scitranslmed.adq4529

#Rett #RettSyndrome #geneTherapy #antisense

`These data set the stage for a potential therapeutic strategy using antisense oligonucleotides to promote isoform switching in patients with RTT who carry partially functioning alleles of MECP2.`

https://www.science.org/doi/10.1126/scitranslmed.adq4529

#Rett #RettSyndrome #geneTherapy #antisense

https://www.europesays.com/uk/366660/ Ionis gets approval for preventing attacks in rare and genetic HAE #Antisense #BioWorld #Dawnzera #Dermatologic #donidalorsen #FDA #GeneticDiseases #Genetics #HereditaryAngioedema #IonisPharmaceuticalsInc. #ProphylacticTherapies #RareDisease #Regulatory #Science #UK #UnitedKingdom

Ionis gets approval for preventing attacks in rare and genetic HAE

In Ionis Pharmaceuticals Inc.’s second U.S. FDA approval in under a year, the agency approved Dawnzera (donidalorsen) as…
#NewsBeep #News #Genetics #Antisense #BioWorld #CA #Canada #Dawnzera #Dermatologic #donidalorsen #FDA #geneticdiseases #hereditaryangioedema #IonisPharmaceuticalsInc. #prophylactictherapies #raredisease #Regulatory #Science
https://www.newsbeep.com/ca/90643/

https://www.europesays.com/uk/103097/ Injecting medicine into amniotic fluid shows promise for treating genetic disorders #amniocentesis #AmnioticFluid #Antisense #Biogen #brain #CentralNervousSystem #Children #Genes #Genetic #Genetics #InUtero #Medicine #MuscularAtrophy #Nerve #NervousSystem #NeurodegenerativeDisease #Oligonucleotides #Research #rna #Science #SpinalMuscularAtrophy #UK #UnitedKingdom

Heutige #Antibiotika zerstören viele Bakterienarten auf einmal, auch nützliche. #Antisense-Antibiotika hingegen vernichten gezielt krankmachende Bakterien. Bei Spektrum erklärt Jörg Vogel, Direktor des Helmholtz-Instituts Würzburg, wie die #RNA-ähnlichen Moleküle wirken und wie sie Nebenwirkungen sowie #Resistenzen verringern können.
http://www.spektrum.de/news/antibiotika-zielgenaue-bakterienkiller-gegen-resistenzen/2141766

#Trump #Tuesday #tRNA #AntiSense https://phys.org/news/2023-04-rna-fragments-productivity-standardization.html

🇪🇺🇳🇱
🧬Looking for a postdoc to test an #antisense #oligonucleotides #FSHD to prevent #DUX4 in #Leiden (NL)

https://t.co/QwnkvUKc5o

🇨🇦
👉Knocking Down DUX4 in Immortalized #FSHD Patient-Derived Muscle Cells

💡#Antisense #oligonucleotides induce efficient #DUX4 transcript knockdown

📰https://pubmed.ncbi.nlm.nih.gov/36401032/

@johnasayer @cilia

Great to see you here and to connect, John! 🙂 Welcome to #ScienceMastodon!
👍

#cilia #ciliopathies #antisense #BBS
#biology